Phase I/II Study of Retroviral-Mediated Transfer of Iduronate-2-Sulfatase Gene Into Lymphocytes of Patients With Mucopolysaccharidosis II (Mild Hunter Syndrome)
PHASE1
OBJECTIVES: I. Evaluate the safety and feasibility of treating mucopolysacc...
Peripheral Blood Stem Cells Obtained From Normal Volunteers for Studying Retroviral Vector Mediated Gene Transfer Into Primitive Hematopoietic Cells and Vector Mediated Transgene Expression in Mature Hematopoietic Lineages
N/A
These studies are designed to evaluate the relative efficiency of gene tran...
Status
Completed
Location
St. Jude Children's Research Hospital
Start Date
2006-10
Trial ID
NCT00758992
Gene Therapy for Gaucher's and Fabry Disease Using Viruses and Blood-Forming Cells
PHASE1
Gaucher's disease is a lysosomal storage disease resulting from glycocerebr...
Status
Completed
Location
National Institute of Neurological Disorders and Stroke (NINDS)